A new system that delivers Brineura (cerliponase alfa) into the brains of people with CLN2 disease, also known as…
Articles by Steve Bryson, PhD
Sex-specific differences in sleep disturbances have been discovered in a mouse model of juvenile Batten disease, according to the…
Drinking acidified laboratory water improved motor performance, restored muscle strength, prevented tremors, and extended survival in a mouse model of…
Researchers have developed a mouse model of juvenile Batten disease that better reflects the survival outcomes of human patients,…
Gene therapy was able to reduce the signs and symptoms of late infantile Batten disease in a mouse model…
Changes in the levels of certain metabolites in the brain among people with juvenile Batten disease, also called CLN3…
A lack of the CLN3 protein — the underlying cause of juvenile Batten disease — impairs the function of…
Regenxbio says it will test RGX-381, its investigational gene therapy for eye problems associated with neuronal ceroid lipofuscinosis…
Neurogene has decided to discontinue its research program focusing on CLN7, a form of late-infantile Batten disease, including…
Researchers have proposed an alternate classification model for Batten disease types based on the site first affected by each…