Roche’s CellCept was safe, but lacked clinical benefits, during short-term use by patients with…
Articles by Ana Pena, PhD
Neuron-like cells derived from a Batten patient’s skin cells may be a suitable way of investigating the…
Therapeutic approaches that target production of a protein called progranulin in specific brain cells may help preserve brain function in…
Research into the CLN3 protein, whose nonfunctional form underlies juvenile Batten disease, may be compromised by…
Several compounds were able to correct defects in the brain caused by juvenile neuronal ceroid…
Chinese researchers used an advanced genetic sequencing technique to identify two new pathogenic variants of the CLN8 gene in…
Gene therapy directly targeting a specific type of neuron in the retina of the eye was able to…