• Cannabis Oil as Add-on Therapy Seen to Ease Severe Seizures in CLN6 Batten
  • Walking the Path From Here to There
  • Enrollment Begins in Natural History Study of 2 Batten Disease Subtypes
  • NORD Push for Rare Disease Advisory Councils Focus of Dec. 16 Public Meeting
  • Juvenile Batten Disease Treatment BBDF-101 Earns FDA’s OK for Pre-Clinical Plan
  • Survey Finds COVID-19 Disrupted Care, Well-Being of Rare Disease Patients in Europe
  • Latest NORD Webinar Offers Insights on Starting Nonprofit, Patient Registry
  • BDFA Seeks Funds for Potential Brineura Study to Try Saving Children’s Sight
  • Giving Thanks, Despite Batten Disease
  • Taysha, Invitae Partner on Rapid Genetic Testing for Lysosomal, Epileptic Disorders
  • NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits
  • Amicus Gene Therapy Effective After 2 Years in CLN6 Batten Children, Interim Results Show