Victoria Tan,  —

Recent Posts

• Regenxbio halts gene therapy programs for late infantile Batten
• Strategies proposed for treating fear episodes in juvenile Batten disease
• RGX-181 gene therapy seen to reduce child’s seizures by over 80%
• Rare diseases conference aims to bring attention to new therapies
• Webinar to tackle challenges in pediatric rare disease trials
• In ‘Blind Momentum,’ Batten disease takes a back seat to bravery
• URMC will use funding boost to bet on Batten gene therapies
• Digital biomarkers may lead to more robust clinical trials for rare diseases
• Regenxbio advancing 2 gene therapies in pipeline for Batten
• Seeking patience in the fight against Batten disease