Recent Posts
- Regenxbio halts gene therapy programs for late infantile Batten
- Strategies proposed for treating fear episodes in juvenile Batten disease
- RGX-181 gene therapy seen to reduce child’s seizures by over 80%
- Rare diseases conference aims to bring attention to new therapies
- Webinar to tackle challenges in pediatric rare disease trials
- In ‘Blind Momentum,’ Batten disease takes a back seat to bravery
- URMC will use funding boost to bet on Batten gene therapies
- Digital biomarkers may lead to more robust clinical trials for rare diseases
- Regenxbio advancing 2 gene therapies in pipeline for Batten
- Seeking patience in the fight against Batten disease