Recent Posts
- Early data support Regenxbio’s gene therapy program for CLN2 disease
- Changes in brain metabolites may be biomarkers for CLN3 disease
- Seizures in protracted CLN3 disease start later, delaying diagnosis: Study
- Grief fueling fury: What it means to fight Batten disease like a mother
- FDA approves Phase 3 trial design to test Batten-1 for juvenile Batten
- Study probes clinical variability from mutations in Batten-linked genes
- Virtual 5K event hopes to raise funds and awareness about Batten disease
- Lack of CLN3 harms the process of survival for cells under stress: Study
- Improvements for my migraines, but what about for Batten disease?
- T-shirt design contest opens for Batten disease awareness day