Recent Posts
- Webinar to tackle challenges in pediatric rare disease trials
- In ‘Blind Momentum,’ Batten disease takes a back seat to bravery
- URMC will use funding boost to bet on Batten gene therapies
- Digital biomarkers may lead to more robust clinical trials for rare diseases
- Regenxbio advancing 2 gene therapies in pipeline for Batten
- Seeking patience in the fight against Batten disease
- Presymptomatic, symptomatic CLN5 sheep aided by gene therapy
- Researchers develop minipig model to study juvenile Batten disease
- Horizon awards grants to 50 rare disease advocacy groups
- Abnormalities in eye tests may help diagnose juvenile Batten: Study