Rachita Narsaria, MD,  —

Recent Posts

• Advice to parents of children with late-infantile Batten disease
• A letter to Juju, my 7-year-old son with Batten disease
• ‘Deprioritized’ gene therapy given as treatment for Batten disease
• So long to ‘The Long Sprint,’ but not my fight against Batten disease
• How a late-infantile Batten disease diagnosis led to advocacy
• Sortilin protein inhibition shows promise as Batten disease treatment
• CLN2 gene therapy shows safety, promising efficacy in monkey study
• Regenxbio halts gene therapy programs for late infantile Batten
• Strategies proposed for treating fear episodes in juvenile Batten disease
• RGX-181 gene therapy seen to reduce child’s seizures by over 80%