In rare cases, a type of Batten disease may appear at birth, write researchers in a case report, describing a…
Articles by Magdalena Kegel
Abnormal processing of the trace element manganese may impact the onset or progression of Batten disease, according to a…
People with Batten disease would likely benefit from early educational interventions that allow them to make up for their lost…
Batten disease may be caused by the loss of synaptic connections between neurons in the brain, according to a study…
Yeast models of Batten disease and other lysosomal storage disorders could speed up the discovery of treatments by overcoming the…
Although Brineura (cerliponase alfa) is now approved both in Europe and the U.S. to treat CLN2 type Batten disease, its clinical trial…
Mouse experiments with a gene therapy for juvenile Batten disease indicate that lower activation of the mutated CLN3 gene are…
Patients with a specific type of Batten disease now have an approved treatment, with the U.S. Food and Drug Administration’s…