A new mutation found in the CTSD gene does not associate with the rare CLN10 form of Batten disease,…
Articles by Forest Ray PhD
Juvenile Batten disease is difficult to diagnose promptly and accurately, as demonstrated by the case of twin girls with…
The European Medicines Agency (EMA) designated Neurogene’s gene therapy candidate for CLN5, a form of late-infantile Batten disease, an…
Regenxbio plans to provide updates on its RGX-181 and RGX-381 gene therapy candidates for late-infantile neuronal…
The two COVID-19 vaccines that recently received emergency approval from the U.S. and other worldwide regulatory agencies are expected…