The inaugural International Batten Disease Awareness Day was launched on June 9 under the theme “Come Together.” It became a milestone…
Articles by Ana de Barros, PhD
A 24-month campaign to raise $6 million toward curing juvenile Batten disease got a $70,000 pop in February, the Beyond Batten…
The inaugural issue of the the CRISPR Journal published an article focusing on the potentials of CRISPR gene therapy in…
BioMarin recently announced the launch of RARE Scholars, an annual scholarship program for students with certain rare diseases, including…
The New York Stem Cell Foundation and the Beyond Batten Disease Foundation are making juvenile Batten disease stem cells available…
Brineura (cerliponase alfa), marketed by BioMarin Pharmaceuticals, was given the WORLDSymposium 2018 New Treatment Award in recognition of its achievements in treating…
A potential gene therapy to treat infantile Batten disease, ABO-202 by Abeona Therapeutics, has been designated an orphan drug by the U.S.
The Beyond Batten Disease Foundation has started a Be A Hero campaign to raise $1 million and public awareness about…
Brineura (cerliponase alfa), the first therapy approved to treat children with Batten disease, received the 2017 “Best of…
Two parents in Springville, Utah, lost three children in three consecutive days this summer to Batten disease, also known…