• Recommendation Against U.K. Coverage of Brineura Jolts Batten Disease Community
  • FDA Names ABO-202, Potential Gene Therapy for Infantile Batten Disease, an Orphan Drug
  • Rare Disease Groups, Patients Differ on ‘Right to Try’ Bill Before US Congress
  • Abnormal Autophagy Is Common in Lysosomal Storage Diseases, Including Batten
  • Early Detection of Retinal Dysfunction May Help Diagnosis
  • NORD Fundraiser Sets 7,000-Mile ‘Bike, Run or Walk’ Goal for 7,000 Rare Diseases
  • Bioinformatic Tool Finds 71% of Batten-causing Mutations in Key Protein Regions
  • Severe Neurodegeneration in Newborn May Be Rare Type of Batten, Case Study Shows
  • FDA Grants PLX-100 Orphan Drug Designation to Treat Batten Disease
  • Mouse Model Helps Researchers Identify Processes Underlying Batten Disease Symptoms
  • Review Suggests Abnormal Manganese Processing May Impact Batten Disease Progression
  • Educational Intervention Needed Early in Batten Patients, Report Suggests