A multicenter Phase 1/2 clinical trial of a gene therapy for CLN7 Batten disease, a form of late-infantile Batten disease, will soon begin in Canada. The trial is being supported by funding that includes $768,823 CAD ($543,326 USD) from Conscience, a Canadian nonprofit focused on drug discovery.
Discussion
There is a loneliness that comes with losing a child that words cannot explain. Since my son Juju gained his wings, the world has kept moving while part of my life has stopped. Some mornings, I forget for a few seconds, then reality returns and breaks my heart again. I’ve…
Becoming educated and informed about Batten disease is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your journey.
There is no cure for Batten disease yet, but there are treatments that can help manage the disease. Learn more about the approved and experimental therapies here.
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