• Rare Disease Patient Groups Unite to Preserve Orphan Drug Tax Credit in US
  • Loss of Synaptic Brain Signaling May Cause Batten Disease, Mouse Study Suggests
  • Batten Organization’s Director Says Scientists Zeroing In on Treatments
  • 12-year-old Spearheading $1 Million Research Fund-raiser for Sister with Batten Disease
  • Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’
  • Brain Cell Function Impaired in Early Forms of Batten Disease, Mouse Study Shows
  • #NORDsummit – Alternatives to Large Placebo Trials, Grant Awards Among Ways FDA Supporting Rare Diseases, Chief Says
  • Brineura, for Batten CLN2, Named One of Year’s Top Health Innovations by Popular Science
  • #NORDsummit – Despite Criticism, Orphan Drug Act Is Working to Advance Needed Treatments, FDA Says
  • Gene Therapy Decreased Protein Aggregates in Animal Model of Batten Disease, Study Finds
  • Collection of Batten Disease Stem Cell Lines Available for Research, Organizations Announce
  • Utah Family Loses 3 Children in 3 Consecutive Days to Batten Disease