• Severe Neurodegeneration in Newborn May Be Rare Type of Batten, Case Study Shows
  • FDA Grants PLX-100 Orphan Drug Designation to Treat Batten Disease
  • Mouse Model Helps Researchers Identify Processes Underlying Batten Disease Symptoms
  • Review Suggests Abnormal Manganese Processing May Impact Batten Disease Progression
  • Educational Intervention Needed Early in Batten Patients, Report Suggests
  • Rare Disease Patient Groups Unite to Preserve Orphan Drug Tax Credit in US
  • Loss of Synaptic Brain Signaling May Cause Batten Disease, Mouse Study Suggests
  • Batten Organization’s Director Says Scientists Zeroing In on Treatments
  • 12-year-old Spearheading $1 Million Research Fund-raiser for Sister with Batten Disease
  • Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’
  • Brain Cell Function Impaired in Early Forms of Batten Disease, Mouse Study Shows
  • #NORDsummit – Alternatives to Large Placebo Trials, Grant Awards Among Ways FDA Supporting Rare Diseases, Chief Says