• Neural Stem Cells from Batten Patients Can Be Used to Test New Therapies, Researchers Say
  • Genome Sequencing Accurately, Rapidly Diagnosed CLN8 Variants in Boy, 8
  • NIH Agency Pioneers Collaborative Research into Rare Diseases
  • Gene Therapy Prevents Vision Loss Caused by CLN6 Disease in Mouse Study
  • Loss of CLN7 Protein Contributes to Development, Progression of Batten Disease, Mouse Study Finds
  • Key Beyond Batten Disease Foundation Fund-raiser Brings in $70,000 in February
  • Inaugural Issue of the CRISPR Journal Features Study About Batten Disease
  • FDA Grants Rare Pediatric Disease Designation to ABO-202 for Infantile Batten Disease
  • Genome Sequencing and Its Clinical Potential Focus of NYC Rare Disease Day Event
  • New Mouse Model and Gene-Editing Tool May Help Advance CLN2 Research
  • ‘A Disease May Be Rare, Hope Should Never Be,’ Says Boy with SMARD at Connecticut Rare Disease Day Event
  • Rare Disease Groups Welcome FDA’s Embrace of ‘Real World’ Data in Clinical Trials